Registered cases


Registered cases

Gender distribution
Gender Count
Male 3
Female 5
# Diagnose names Count
1 glutaric aciduria type ll 2
23-Hydroxy-3-methylglutarylCoA lyase deficiency0
33-HydroxyacylCoA dehydrogenase(Short-chain 3- HydroxyacylCoA dehydrogenase) Deficiency2
43-Methylglutaconic aciduria (MGA)2
53methylcrotonyl glycinuria1
64Hydroxybutyric aciduria0
7?- Pyrroline-5-Carboxylase Reductase deficiency1
8Adenylosuccinate lyase deficiency(ADSL)1
9Adrenoleukodystrophy19
10Alexander Disease1
11Alfa-Mannosidosis0
12Alkaptonuria0
13Argininemia0
14Argininosuccinic aciduria0
15Aromatic L-Amino acid Decarboxylase Deficiency (AADC)1
16Ataxia Telangectasia1
17Ataxia with Oculomotor Apraxia Type 1 (AOA1)5
18Biotin-Thiamine- Responsive B6 Disease2
19Biotinidase deficiency21
20Branched Chain Ketoacid dehydrogenase kinas deficiency(BCKDK)3
21Canavan8
22Carbamylphosphate synthetase deficiency0
23Carnitine -acylcarnitine translocase deficiency0
24Carnitine palmitoyl transferase l deficiency0
25Carnitine palmitoyl transferase ll deficiency,late onset0
26Carnitine palmitoyl transferase ll deficiency,lethal neonatal0
27Carnitine transporter deficiency1
28Citrullinemia1
29Cobalamin G1
30CoblC- CoblG- CoblF8
31Cockayne syndrome0
32Combined oxidation phosphorylation deficiency 6 (cow check syndrome)4
33Congenital Disorder of glycosilation0
34Creatine Deficiency 1
35Cystinosis0
36Cystinuria0
37D-2-Hydroxyglutaric aciduria4
38Deficiency of the pyruvate dehydrogenase complex0
39Developmental and epileptic Encephalopathy1
40Dihydropyrimidine dehydrogenase deficiency1
41Dual specificity tyrosine phosphorylation regulate kinase 21
42ethylmalonic - adipic aciduria0
43Ethylmalonic encephalopathy (EE)2
44Fabry disease0
45Familial hypercholesterolemia0
46Focal cortical dysplasia II1
47Fructose-1,6-biphosphatase deficiency2
48Fucosidosis0
49Galactosemia0
50Galactosialidosis0
51Gaucher disease0
52GHMP KINASE1
53glucose transporter1 deficiency2
54Glutamine synthetase deficiency0
55Glutaric aciduria type l20
56Glutaric aciduria type ll1
57Glycogen storage diseases0
58Glycogenosis type 1- Von Gierke disease0
59Glycogenosis type 2 /Pompe2
60Glycogenosis type 3 0
61Glycogenosis type 3 / amylo-10
62Glycogenosis type 40
63Glycogenosis type 50
64Glycogenosis type 60
65Glycogenosis type 70
66GM1 gangliosidosis (Juvenile)2
67GM1 gangliosidosis type I (Infantile-Late)4
68GM1 gangliosidosis type II 0
69GM2 activator deficiency2
70GM2 gangliosidosis(Sandhoff disease)1
71GM2 gangliosidosis(Tay-sachs disease)3
72Hartnup disease0
73hepatorenal tyrosinemia0
74HIBCH deficiency1
75holocarboxylase synthetase deficiency0
76homocisteine transferase deficiency1
77Homocystinuria4
78Hunter disease1
79Hurler disease0
80Hyper phosphatasia2
81Hyperornithinemia1
82Hyperornithinemia-hyperammonemia-homocitrullinuria syndrome (HHH)1
83Hyperphenylalaninemia0
84Hypoglycemia occipital-lobe-epilepsy syndrome1
85isovaleric acidemia5
86joubert syndrome0
87Keans-Sayre syndrome0
88Krabbe disease4
89L-2 Hydroxyglutaric aciduria5
90l-cell disease/mucolipidosis ll0
91LAFORA DISEASE1
92Leigh syndrome5
93Lesch-Nyhan disease and variants0
94Leukodystrophy0
95Long chain L-3-hydroxyacyl CoA dehydrogenase-(trifunctional protein deficiency)0
96Lysinuric protein intolerance0
97Maple syrup urine disease(MSUD)3
98Maroteaux-Lamy disease/mucopolysaccharidosis Vl0
99Medium chain acyl CoA dehydrogenase deficiency(MCAD)3
100Menkes disease1
101Metachromatic leukodystrophy(MLD)8
102methyl malonic semialdehyde dehydrogenase deficiency1
103Methylmalonic acidemia22
104methylmalonic aciduria and homocystinuria(Cobalamin C Deficiency)16
105methylmalonic aciduria and homocystinuria(Cobalamin E Deficiency)0
106methylmalonic aciduria and homocystinuria(Cobalamin G Deficiency)1
107Mevalonic aciduria2
108Mitochondrial acetoacetyl-CoA thiolase(3-oxothiolase)deficiency0
109Mitochondrial cytochrome c oxidase (COX) deficiency2
110Mitochondrial DNA Deptetion syndrom 71
111Mitochondrial dysfunction19
112Mitochondrial encephalomyelopathy,lactic acidosis,and stroke-like episodes(MELAS)2
113Mitocondrial DNA Depletion Syndrome 2 (MTDPS2)3
114Molybdenum cofactor Deficiency2
115Morquio syndrome/mucopolysaccharidosis type lV1
116Mucolipidosis0
117Mucolipidosis lll0
118Multiple acyl CoA dehydrogenase deficiency/ Glutaric aciduria type II/ ethylmalonic-adipic aciduria1
119Multiple carboxylase deficiency /holocarboxylase synthetase deficiency0
120Multiple sulfatase deficiency1
121Myoclonic epilepsy and ragged red fiber(MERRF)disease0
122Neonatal adrenoleukodystrophy0
123Neonatal Ceroid Lipofuscinosis(NCL)7
124Neurodegeneration with Brain Iron Accumulation(NBIA)1
125Neurodegeneration.ataxia,and retinitis pigmentosa(NARP)0
126Neurodegeneration.ataxia,and retinitis pigmentosa(NARP)1
127Neurodegenerative disorder2
128Neuropathy,Russse type1
129Neurotransmitter Disorder2
130Niemann-pick A/B disease1
131Niemann-pick type C disease19
132Nonketotic hyperglycinemia0
133NOTCH3(Cerebral artropathy with subcortical infarcts and leukoencephalopathy1)0
134OBESITY1
135oculocutaneous tyrosinemia0
136Ornithine transcarbamylase deficiency1
137Orotic aciduria2
138oxothiolase deficiency1
139Pearson syndrome0
140phenylketonuria6
141Pontocerebellar hypoplusia1
142Propionic acidemia3
143Pyruvate carboxylase deficiency0
144Pyruvate Dehydrogenase deficiency1
145Sandhoff disease11
146Scheie and Hurler-Scheie diseases0
147Short-chain acyl CoA dehydrogenase deficiency0
148Sly disease0
149Succinate Dehydrogenase Deficiency4
150Tay-sachs disease3
151The mitochondrial DNA depletion syndromes0
152Thiamine Dysfunction2
153Thiamine Responsive Megaloblastic Anemia(TRMA Anemia)1
154Tyrosinemia2
155vanishing white mather1
156Very long chain acyl CoA dehydrogenase deficiency0
157Wolman disease0
158Zellweger6